Infant in England first to receive life-saving drug for spinal muscular atrophy

Five-month-old Arthur Morgan has become the first patient in England to receive a life-saving treatment that can prolong the lives of children with spinal muscular atrophy (SMA), a progressive disorder that causes loss of muscle control. The treatment could enable babies with SMA to sit, crawl, and walk—which would have been impossible just years ago. Left … Continue reading Infant in England first to receive life-saving drug for spinal muscular atrophy